The assessment of Orkambi® continues today as The National Institute for Health and Care Excellence (NICE) takes evidence from people with cystic fibrosis, clinical experts and the drugs manufacturer Vertex Pharmaceuticals Ltd.
Parent and grandparents of people with cystic fibrosis and supporters of the Trust gathered in London on Tuesday for an update on the Trust’s vision for a life unlimited by cystic fibrosis for everyone born with the condition.
Experts in gastrointestinal (GI) health from across Europe came together at the Trust’s latest research ‘sandpit’ last week to explore innovative approaches to complications in the GI tract, one of the major causes of ill health faced by people with cystic fibrosis.