Following the announcement that Kaftrio has been approved for use for eligible children aged 6-11 in Northern Ireland, we are delighted that the MHRA has also now approved the life-changing CF drug for children across the rest of the UK too. This is a huge milestone in the Kaftrio journey following years of campaigning by people with cystic fibrosis and their families.
The life-changing cystic fibrosis drug, Kaftrio, has been approved for use for eligible children aged 6-11 in Northern Ireland. This is a huge milestone in the Kaftrio journey following years of campaigning by people with cystic fibrosis and their families.
A group of charities, including the Trust, have published a letter for everyone who is at highest risk from COVID-19 to download and use in discussion with your employers about how to keep safe at work.
Dr Mike Gray's Strategic Research Centre is working to understand more about alternative drug targets to CFTR to develop disease modifying treatments for cystic fibrosis.
We are determined to find life-changing treatments that work for everyone, so that no one in our community is left behind. In our latest Research in Focus report, we spotlight the exciting Trust-funded research underway into 'alternative ion channels' and the development of medicines that could work for everybody with CF.
This could make a big difference for families like Lizzy’s, whose 16-year-old son Isaac has a rare type of CF which means he does not benefit from CFTR modulator drugs like Kaftrio. Here, Lizzy shares their story.
We update you on progress that’s been made in addressing your research priorities in the last five years, and why we’ll be asking for your help in refreshing them in the New Year.
COVID-19 remains a threat, particularly to some groups such as transplant recipients and other immunosuppressed people. This research study will help scientists and the Government assess the effectiveness of the third COVID-19 vaccination or “booster” vaccination programme among immunosuppressed people. A 6 month follow up will see how many Covid infections have been reported in the trial groups. If you’ve had a solid organ transplant (e.g. lung, liver, kidney), are taking medication to suppress your immune system and have received your third COVID-19 vaccination or “booster” vaccination, you can register to take part. Visit www.melodystudy.org to find out more about...