While we await clarification on mutation listings for approved use of Kaftrio, we’ve received many questions about the progress of CFTR modulator trials for people with cystic fibrosis (CF) who do not meet the initial criteria. Here, our Clinical Trials team explains how access to new modulator medicines begins with clinical trials.
A round up of news from the campaign for access to medicines, including MSPs meeting in Scotland, negotiations in England, a potential debate in Wales and a protest gathering in Northern Ireland.
On this day thirty years ago, two scientific reports were published describing the CFTR gene, the gene that causes cystic fibrosis (CF). Its discovery led to advances in the care and treatment of people with CF, but some of its secrets are still to be uncovered. Here are five things that are happening as a result of those important reports.
Emma Lake, Community Manager at the Trust, tells us how she's getting on top of her health and taking up a long-lost hobby by joining 24 Hours for CF this summer.
Inspired by the Herculean efforts of Josh Llewellyn-Jones, Anna Bennett and a group of family and friends took part in the 24 Hours for CF challenge this August, raising over £3,500 for Cystic Fibrosis Trust. Here, she tells us all about her incredible exercise journey, and how it helped her after her daughter's diagnosis.