Drug manufacturer Vertex has submitted a proposal to NHS England for access to its current and future CF treatments. The offer, described by Vertex as a ‘portfolio approach’, is similar to that adopted in the Republic of Ireland, and covers not just Orkambi but also future drugs in the pipeline – including new combination therapy Symdeko (tezacaftor/ivacaftor).
Following a request from the Cystic Fibrosis Trust, Orkambi manufacturer Vertex has issued a statement on proposals to increase access to Orkambi and other pipeline drugs, and outlined the next steps for the four UK nations.
Following a meeting with Orkambi manufacturer Vertex on Monday, David Ramsden, the Cystic Fibrosis Trust’s Chief Executive, has issued a statement demanding action and backing a community-led petition to the Government.
As Vertex announces trials for new treatments that could benefit more than 90% of people with cystic fibrosis (CF) in the UK, Dr Belinda Cupid, Senior Impact Adviser at the Trust, takes a closer look.
Today Vertex Pharmaceuticals has announced that the European Medicines Agency (EMA) has validated a marketing-authorisation application for the triple combination Trikafta (elexacaftor, tezacaftor and ivacaftor), meaning that the EMA will carry out a scientific assessment of the application and make a recommendation on whether the medicine should be marketed within the EU or not.
This Valentine’s Day, meet Chris, who has cystic fibrosis, and Michaela, who have been married for a year and a half and have a two and a half year old son, Elliott. We spoke to them about their experiences taking part in the Great North Run together and how going through the ups and downs of CF treatments and hospital admissions has taken their relationship from strength to strength.
This Valentine's Day we're exploring love and cystic fibrosis. Here, proud wife Nicola tells us about her experience of falling in love with someone with cystic fibrosis.
This Valentine's Day we're exploring love and cystic fibrosis. Here, proud husband Gearoid tells us about his experience of falling in love with someone with cystic fibrosis.
